COLUMBUS, Ohio (WCMH) – It’s being called a pioneering event that holds great promise for children who have Duchenne muscular dystrophy. After decades of research, animal studies, and human trials, ...

In research published in Developmental Medicine & Child Neurology, investigators have developed a brief, reliable, and valid ...

A diagnosis of Duchenne muscular dystrophy (DMD) can come as a shock to parents and caregivers. Resources and support from family and friends can help you and your child navigate the diagnosis and ...

In a landmark moment for the Abigail Wexner Research Institute at Nationwide Children's, a 5-year-old from Bellefontaine, Ohio, received the first dose of a recently approved gene therapy for Duchenne ...

Muscle tissue damage appears when muscular dystrophy is induced in a mouse model (middle). But when researchers block the function of two genes that drive unwanted mitochondrial pore formation (right) ...

WASHINGTON, June 12, 2025 /PRNewswire/ -- Parent Project Muscular Dystrophy (PPMD), a nonprofit organization leading the fight to end Duchenne muscular dystrophy (Duchenne), is pleased to announce the ...

An Australian-first biobank will be established to improve and discover new treatments for children with genetic muscle diseases. These diseases, spanning dystrophies and myopathies, are characterised ...

Little Mix alum Jesy Nelson opened up in an emotional video Jan. 4 about her twin daughters’ Spinal Muscular Atrophy Type 1 diagnosis, a life-threatening disease that leads to severe muscle weakness.

British singer Jesy Nelson recently took to Instagram to share a devastating update about her 8-month-old twin daughters.

The greatest reduction in skeletal muscle mass was in the lower extremities, a new report shows. Low skeletal muscle mass may be an early manifestation of fabry disease (FD), according to a new report ...

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